首页> 中文期刊> 《亚洲药物制剂科学(英文)》 >Feasibility study of cyclodextrins as active pharmaceutical ingredients for the treatment of GM1-gangliosidosis

Feasibility study of cyclodextrins as active pharmaceutical ingredients for the treatment of GM1-gangliosidosis

         

摘要

GM1-gangliosidosis is a rare lysosomal storage disorder characterized clinically by a wide range of variable neurovisceral,ophthalmological and dysmorphic features. Without enough functionalβ-galactosidase, GM1-gangliosides cannot be degraded in lysosomes, and accumulate to toxic levels in many tissues and organs, particularly in the brain. In spite of several approaches for the treatment of GM1-gangliosidosis.

著录项

  • 来源
    《亚洲药物制剂科学(英文)》 |2016年第1期|P.183-184|共2页
  • 作者单位

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [2]Program for Leading Graduate Schools“HIGO(Health life science:Interdisciplinary and Glocal Oriented)Program”;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [3]Center for Animal Resources and Development;

    Kumamoto University;

    2-2-1 Honjo;

    Chou-ku;

    Kumamoto;

    Japan;

    [3]Center for Animal Resources and Development;

    Kumamoto University;

    2-2-1 Honjo;

    Chou-ku;

    Kumamoto;

    Japan;

    [3]Center for Animal Resources and Development;

    Kumamoto University;

    2-2-1 Honjo;

    Chou-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [2]Program for Leading Graduate Schools“HIGO(Health life science:Interdisciplinary and Glocal Oriented)Program”;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [4]Institute of Molecular Embryology and Genetics;

    Kumamoto University;

    2-2-1 Honjo;

    Chou-ku;

    Kumamoto;

    Japan;

    [1]Graduate School of Pharmaceutical Sciences;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

    [2]Program for Leading Graduate Schools“HIGO(Health life science:Interdisciplinary and Glocal Oriented)Program”;

    Kumamoto University;

    5-1 Oe-honmachi;

    Chuo-ku;

    Kumamoto;

    Japan;

  • 原文格式 PDF
  • 正文语种 CHI
  • 中图分类 药理学;
  • 关键词

    Cyclodextrins; GM1-gangliosidosis; Fibroblasts; Lysosomes;

    机译:环糊精;GM1-神经节苷脂;成纤维细胞;溶酶体;
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