Gene Therapy for Blinding Eye Diseases: The Path to Clinical Success, by the Washington Advisory Group, is the sixth in a series of symposium reports on translating research results more quickly into effective treatments for potentially blinding diseases. The central theme of the report is ocular gene therapy, and it emphasizes recent preclinical studies, the phase-1 clinical trials in progress, plans for further trials, and the challenges and opportunities for moving the field of medical research into clinical applications that have the potential to offer new hope to patients with blinding eye diseases.
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