...
机译:Supply-side and trickle-down therapy (comment)
Children's Hospital Research Foundation, Division of Human Genetics, Cincinnati, Ohio 45229-3039, USA.;
beta-N-Acetylhexosaminidase; Glycosphingolipids; Lysosomal Storage Diseases; β-N-乙酰氨基己糖苷酶; 糖苷神经鞘脂类; 溶酶体累积疾病; N-乙酰氨基半乳糖转移酶类;