机译:Manipulation of Developmental Gamma-Globin Gene Expression: an Approach for Healing Hemoglobinopathies
Christian Med Coll & Hosp;
hemoglobinopathies; gene editing; hematopoietic stem cells; NONDELETIONAL HEREDITARY PERSISTENCE; HEMATOPOIETIC STEM-CELLS; DISTAL CCAAT MOTIF; FETAL-HEMOGLOBIN; BETA-THALASSEMIA; MOLECULAR-BASIS; CELLULAR-DISTRIBUTION; CLINICAL SEVERITY; GENOMIC DNA; MUTATION;