机译:Gene Therapy for Hemoglobinopathies Beta-Thalassemia, Sickle Cell Disease
Bluebird Bio Inc;
National Institutes of Health (NIH) - USA,NHLBI;
Sickle cell disease; Beta-thalassemia; Gene therapy; Gene editing; Lentiviral vector; HEMATOPOIETIC STEM; HEREDITARY PERSISTENCE; PLERIXAFOR; COLLECTION; MOBILIZATION; TRACKING; REVEALS; RISK; SAFE; TIME;