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SPINOCEREBELLAR ATAXIA TYPE 31 INHIBITOR
SPINOCEREBELLAR ATAXIA TYPE 31 INHIBITOR
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机译：脊柱神经性AXAXIA 31型抑制剂
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摘要
The purpose of the present invention is to provide a spinocerebellar ataxia type 31 inhibitor in which an active ingredient is a small-molecule compound that directly acts on, and thereby mitigates the toxicity of, the repeat RNA that is a cause of spinocerebellar ataxia type 31. The spinocerebellar ataxia type 31 inhibitor according to the present invention is characterized by comprising a compound represented by formula (I) as an active ingredient. [In the formula, X and Y independently represent, for example, a =N- group, Z represents an m-valent linker group that bonds m structures in the brackets to each other, m represents an integer of 2-4, α represents a substituent, and l represents an integer of 0-4.]
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