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USE OF PHARMACOLOGICAL CHAPTERONES FOR THE TREATMENT OF LYSOSOMAL DEPOSIT DISEASES (Machine-translation by Google Translate, not legally binding)
USE OF PHARMACOLOGICAL CHAPTERONES FOR THE TREATMENT OF LYSOSOMAL DEPOSIT DISEASES (Machine-translation by Google Translate, not legally binding)
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机译：使用药理学术语治疗溶酶体沉积病（由Google翻译进行机器翻译，不具有法律约束力）
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摘要
Use of pharmacological chaperones for the treatment of lysosomal storage diseases. The invention relates to the use of galactose analogs of the formula (I) which have the ability to stabilize the structure of the α -GalA enzyme, to treat lysosomal storage diseases and, in a preferred embodiment, to treat the disease of Fabry. The present invention also relates to pharmacological compositions comprising an effective amount of at least one of the galactose analogues described herein for treating depot lysosomal diseases and, in a preferred embodiment, for treating Fabry disease. (Machine-translation by Google Translate, not legally binding)
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