首页> 外国专利> METHODS AND COMPOSITIONS FOR REDUCING TACTILE DYSFUNCTION AND ANXIETY ASSOCIATED WITH AUTISM SPECTRUM DISORDER, RETT SYNDROME, AND FRAGILE X SYNDROME

METHODS AND COMPOSITIONS FOR REDUCING TACTILE DYSFUNCTION AND ANXIETY ASSOCIATED WITH AUTISM SPECTRUM DISORDER, RETT SYNDROME, AND FRAGILE X SYNDROME

机译:减少触觉功能障碍和自闭症谱系障碍,RETT综合征和脆性X综合征相关的方法和成分

摘要

The present invention features a method of reducing tactile dysfunction or anxiety in a subject diagnosed with Autism Spectrum Disorder, Rett Syndrome, or Fragile X syndrome by administering a GABAA agent having reduced blood brain barrier or by expressing a nucleic acid encoding an exogenous alpha or beta subunit of a GABAA receptor in dorsal root ganglion neurons in the subject using a vector.
机译:本发明的特征在于一种通过给予具有降低的血脑屏障的GABAA剂或通过表达编码外源性α或β的核酸来减少诊断为自闭症谱系障碍,瑞特综合征或脆性X综合征的受试者的触觉功能障碍或焦虑的方法。使用载体在受试者的背根神经节神经元中的GABA A受体的亚基。

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