首页> 外国专利> Methods and pharmaceutical compositions for the treatment of cardiomyopathy due to friedreich ataxia

Methods and pharmaceutical compositions for the treatment of cardiomyopathy due to friedreich ataxia

机译:治疗弗里德赖希共济失调所致心肌病的方法和药物组合物

摘要

A method for preventing or treating cardiomyopathy due to energy failure in a subject in need thereof is provided. The method comprises administering to the subject a therapeutically effective amount of a vector which comprises a nucleic acid sequence encoding a gene that can reverse energy failure. An exemplary cardiomyopathy is that which is associated with Friedreich ataxia and an exemplary nucleic acid sequence comprises a nucleic acid that encodes frataxin (FXN).
机译:提供了一种在有需要的受试者中预防或治疗由于能量衰竭而引起的心肌病的方法。该方法包括向受试者施用治疗有效量的载体,该载体包含编码可逆转能量衰竭的基因的核酸序列。示例性的心肌病是与弗里德赖希共济失调相关的心肌病,示例性的核酸序列包括编码frataxin(FXN)的核酸。

著录项

相似文献

  • 专利
  • 外文文献
  • 中文文献
获取专利

客服邮箱:kefu@zhangqiaokeyan.com

京公网安备:11010802029741号 ICP备案号:京ICP备15016152号-6 六维联合信息科技 (北京) 有限公司©版权所有
  • 客服微信

  • 服务号