TREATMENT OF CYSTIC FIBROSIS BY DELIVERY OF NEBULIZED MRNA ENCODING CFTR

• 1. 藻酸盐低聚物在治疗囊性纤维化和与缺陷性CFTR离子通道功能相关的其它疾病中的应用 [P] . 中国专利： CN106029079A . 2016-10-12
• 2. 用于治疗囊性纤维化的CFTR修饰基因和表达的多肽以及检测和/或鉴定它们的方法和产品 [P] . 中国专利： CN1671734A . 2005-09-21
• 3. TREATMENT OF CYSTIC FIBROSIS BY DELIVERY OF NEBULIZED mRNA ENCODING CFTR [P] . 美国专利： US2020157157A1 . 2020-05-21

  机译： 转运CFTR编码的mRNA治疗囊性纤维化

• 4. TREATMENT OF CYSTIC FIBROSIS BY DELIVERY OF NEBULIZED mRNA ENCODING CFTR [P] . 世界知识产权组织专利： WO2020106946A1 . 2020-05-28

  机译： 转运CFTR编码的mRNA治疗囊性纤维化

• 5. TREATMENT OF CYSTIC FIBROSIS BY DELIVERY OF CODON-OPTIMIZED MRNA ENCODING CFTR [P] . 欧洲知识产权局专利： EP3624824A1 . 2020-03-25

  机译： 通过递送编码CFTR的密码子优化的mRNA来治疗囊性纤维化

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• 6. Intra-amniotic Delivery of CFTR-expressing Adenovirus Does Not Reverse Cystic Fibrosis Phenotype in Inbred CFTR-knockout Mice [O] . Suzanne MK Buckley, SN Waddington, S Jezzard, 2008

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