机译:Silence superoxide dismutase 1 (SOD1): a promising therapeutic target for amyotrophic lateral sclerosis (ALS)
Univ Milan, Dino Ferrari Ctr, Neurosci Sect, Dept Pathophysiol & Transplantat DEPT, Milan, Italy;
Amyotrophic lateral sclerosis; ALS; superoxide dismutase 1; SOD1; gene silencing; RNA interference; antisense oligonucleotides; CRISPR; Cas9;