机译:Fostamatinib (tavlesse0) in refractory chronic immune thrombocytopenia Increases platelet count in some patients, but no demonstrated efficacy with respect to bleeding
机译:Tucatinib (tukysa0) in HER2-positive breast cancer, after failure of several HER2-directed drugs Longer survival, but with a high incidence of serious adverse effects and drug interactions
机译:Pegvaliase (palynziq0) in phenylketonuria Reduction in blood phenylalanine levels, but no demonstrated clinical efficacy, plus anaphylactic reactions